Scientists report of a new prototype drug, designed to treat Duchenne muscular dystrophy but which may be useful in the treatment of up 1800 different genetic diseases. The drug, called PTC124, has...
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A preliminary clinical trial has demonstrated that an intravenuously administered nanoparticle containing the FUS1 gene shows clinical activity in stage 4 lung cancer patients. FUS1 can induce...
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In addition to surgery, radiation and chemotherapy, there may now be an additional treatment modality for cancers: dual gene therapy. In a preclinical study, two tumor-suppressing genes, packaged in a...
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